研究单位：[1]Biogen[2]Peking Union Medical College Hospital,Beijing,Beijing,China,100730[3]The First Affiliated Hospital of Fujian Medical University,Fuzhou,Fujian,China,350005[4]Peking University Shenzhen Hospital,Shenzhen,Guangdong,China,518000[5]The Second Hospital of Hebei Medical University,Shijiazhuang,Hebei,China,050000[6]The First Affiliated Hospital of Nanchang University,Nanchang,Jiangxi,China,330006[7]Qilu Hospital of Shandong University,Jinan,Shandong,China,250012[8]West China Hospital, Sichuan University,Chengdu,Sichuan,China,610041[9]The First People's Hospital of Yunnan Province,Kunming,Yunnan,China,650032
研究目的：
The primary objective of the study is to describe the natural history and utilization of disease modifying therapy (DMT) among adult Chinese participants with SMA linked to chromosome 5q (5q-SMA).
